NICE Approves Gene Therapy for Sickle Cell: A B...

By João L. Carapinha

February 4, 2025

Are we on the brink of a cure for sickle cell disease? NICE recently announced the approval of a one-off gene therapy sickle cell for severe sickle cell disease. Epidemiology of Sickle Cell Disease Sickle cell disease affects a signific...